Reports to: VP, US Medical Affairs & Patient Advocacy
About This Role:
The Senior Director, Medical Affairs, Neuromuscular Team will lead the development and execution of the US medical strategy for givinostat in Duchenne muscular dystrophy. The qualified candidate will serve as a key medical representative in the US, supporting external medical expert engagement and development, communication and evidence generation strategy, and cross-functional collaboration.
What You'll Do:
- Be responsible for execution of the US Neurometabolic Medical Affairs strategy aligned with corporate objectives and product lifecycle needs.
- Implement and oversee the execution of US medical plans for Duvyzat, ensuring integration of regulatory, clinical, commercial and global medical perspectives.
- Lead and development the U.S. Neuromuscular Medical Affairs team, including Medical Science Liaisons (MSLs).
- Oversee the execution of medical education, scientific exchange, and non-registrational evidence-generation initiatives.
- Act as a strategic thought partner across Medical Affairs, R&D, and commercial teams.
- Provide medical and scientific support for late-stage clinical development programs, ensuring alignment with business and regulatory strategies.
- Support training and development of internal teams on product science and disease education.
- Implement right-sized systems and processes to optimize effectiveness of the medical affairs neurometabolic organization
- Establish and maintain strong, trusted relationships with external medical experts, academic institutions, and medical societies.
- Oversee a comprehensive medical KOL engagement and insights-generation strategy.
- Localize medical information and publication resources.
- Develop medical governance frameworks to maintain high ethical and compliance standards in all engagements.
Required Skills:
- Advanced degree required (PharmD, MD, or PhD; PharmD strongly preferred).
- Minimum 10 years of progressive experience in U.S. Medical Affairs within the pharmaceutical or biotechnology industry.
- Prior leadership of cross-functional medical teams, including MSLs and medical communications.
- Experience in rare diseases, neurology, or neuromuscular disorders is strongly preferred.
- Deep knowledge of U.S. medical, regulatory, and pharmacovigilance standards.
- Demonstrated ability to work in a fast-paced, evolving environment and to build highly effective and accountable teams from the ground up.
- Experience supporting an early marketed product.
- Collaborative and decisive leader with a proven ability to navigate and contribute effectively within a matrixed organization.
- Exceptional interpersonal skills with a demonstrated ability to build strong relationships with both internal stakeholders and external partners.
Additional Information:
The base compensation range for this role is: $290,000 - $320,000. Compensation is determined through an analytical approach utilizing a combination of factors including, but not limited to, relevant skills & experience, job location, and internal equity.